The University of Sydney, Australia - Gene therapy saves the sight of Australians with eye disease [Revolutionary therapy holds hope for other conditions]

Title:

Gene therapy saves the sight of Australians with eye disease

 

Published:

The University of Sydney, 8 October 2021

https://www.sydney.edu.au/news-opinion/news/2021/10/08/new-gene-therapy-saves-the-sight-of-children-with-eye-disease--.html

 

From the news article:

The ocular gene therapy, LUXTURNA, is the world’s first approved gene replacement therapy for an inherited blinding eye condition and one of the first gene replacements for any human disease. Approved by the Therapeutic Goods Administration, LUXTURNA is used to treat children and adults with biallelic pathological mutations in RPE65, a rare mutation that leads to vision loss and blindness.